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Trials with new drug - Rozrolimupab

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14 years 11 months ago #8814 by Birgitta-A
Trials with new drug - Rozrolimupab was created by Birgitta-A
Hi All,
We have not heard anything about new drugs like AKR 501 or LGD 4665 for a long time. Now a new drug - Rozrolimupab - is tested in Phase II trials tinyurl.com/3xj637b
Kind regards
Birgitta-A
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14 years 11 months ago #8821 by server
Replied by server on topic Re:Trials with new drug - Rozrolimupab

Primary Immune Thrombocytopenia (previously called Idiopathic Thrombocytopenic Purpura) (ITP) is a rare, chronic and debilitating autoimmune disorder associated with increased bleeding risk and impaired quality of life. The primary cause of long-term morbidity and mortality in patients with ITP is hemorrhage (1). The prevalence of ITP in the United States is estimated to be 34,200.


I thought this was quite interesting. We have an new name for our disorder? And only 34,200 of us are out there? hmmmmmmm.

edit: 34,200, in the US.
My flesh and my heart may fail, but God is the strength of my heart and my portion forever.
Psalm 73:26
Blessings,
gretchen
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14 years 11 months ago #8830 by HSheppard
Replied by HSheppard on topic Re:Trials with new drug - Rozrolimupab
Very interesting! I don't know about you, but I don't feel "debilitated". Impaired quality of life maybe, but not debilitated!
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14 years 11 months ago #8832 by HSheppard
Replied by HSheppard on topic Re:Trials with new drug - Rozrolimupab
Very interesting! I don't know about you, but I don't feel "debilitated". Impaired quality of life maybe, but not debilitated!
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  • Sandi Forum Moderator Diagnosed in 1998, currently in remission. Diagnosed with Lupus in 2006. Last Count - 344k - 6-9-18
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14 years 11 months ago #8835 by Sandi
Replied by Sandi on topic Re:Trials with new drug - Rozrolimupab
Yeah, there seems to be a bit of misinformation there. Those statements are misleading to say the least.
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14 years 11 months ago #8844 by SteveC
Replied by SteveC on topic Re:Trials with new drug - Rozrolimupab
Sounds like marketing/pr speak for this is so important you've got to support us :)
Blessings of enough...
Faith to trust our Lord
Joy to share with others
Strength to help the weak
Love to share with the hurting

Steve C
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14 years 11 months ago #8855 by Bunnie
Replied by Bunnie on topic Re:Trials with new drug - Rozrolimupab

An FDA Orphan Drug designation provides tax benefits and an exemption from user fees, eligibility for grant funding, the opportunity of protocol assistance, the possibility to receive a fast track and expedited review process, as well as a seven-year period of market exclusivity after product approval


Good news/bad news... Likely they are using a very narrow definiton of people who qualify as "ITP". If they make the numbers higher then they may not qualify for the special designation which makes it possible for them to fast track and make money.
If it helps, then we want it on the market ASAP. On the other hand, once it's on the market they get additional protection to keep the cost high without competion.
"I am an old man and have known a great many troubles, but most of them have never happened.\" — Mark Twain\\\\\\"Worry is a misuse of the imagination.\" — Dan Zadra
14 years 11 months ago #8877 by
Replied by on topic Re:Trials with new drug - Rozrolimupab

If it helps, then we want it on the market ASAP. On the other hand, once it's on the market they get additional protection to keep the cost high without competion.

But isn't this how Promacta and Nplate were developed and marketed? Without the orphan disease program, we might not have those two treatment options at all.
Personally, I have no problem at all with pharmaceutical companies recouping part of the huge amounts of capital which they invest in R&D to create new drugs specifically designed to treat just one oddball disease.
Unlike Prednisone, which pretty much "treats most anything for pennies"...as long as you can stand taking the stuff. ;)
.
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14 years 11 months ago #8889 by Bunnie
Replied by Bunnie on topic Re:Trials with new drug - Rozrolimupab
I don't disagree that pharmaceutical companies should make a profit or recoup their capital. And if you have insurance or are low enough income to qualify for the pharmaceutical aid, the costs can be managed. However, there will be individuals in the USA who will not meet those criteria or countries with national health programs that will see delays before they can begin using them. Like I said, good news/bad news.
"I am an old man and have known a great many troubles, but most of them have never happened.\" — Mark Twain\\\\\\"Worry is a misuse of the imagination.\" — Dan Zadra
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